It is treatable
Through ALD Newborn Screening, affected children have the opportunity to benefit from lifesaving treatment. While treatment through a cord blood/stem cell transplant can slow the progression of the disease, it is not considered a cure. Unfortunately, myelin that has already been damaged cannot be repaired by this treatment. This is why it is important for ALD disease to be detected as early as possible before symptoms begin, ideally through each state including ALD in their newborn screening program.